What Is Gene Therapy and How Does It Work?
Gene therapy represents a groundbreaking approach in medicine, focusing on correcting genetic defects at their source rather than merely treating symptoms. By delivering new or corrected genes via safe carriers, gene therapy targets diseases caused by faulty genes, potentially offering lasting cures. With advancements such as CRISPR, therapies like Luxturna and Zolgensma highlight its promise, though challenges like high costs, immune responses, and ethical concerns remain.


